Company Description
PTC Therapeutics, Inc., a biopharmaceutical company, focuses on the discovery, development, and commercialization of medicines to children and adults living with rare disorders in the United States and internationally.
The company offers Translarna and Emflaza for the treatment of Duchenne muscular dystrophy; Upstaza to treat aromatic l-amino acid decarboxylas (AADC) deficiency, a central nervous system disorder; Tegsedi and Waylivra for the treatment of rare diseases; and Evrysdi to treat spinal muscular atrophy (SMA) in adults and children.
Its development pipeline products include Sepiapterin for the treatment of phenylketonuria; PTC518 splicing platform, which is being developed for the treatment of Huntington’s disease; and inflammation and ferroptosis platforms, including vatiquinone to treat Friedreich’s ataxia.
The company distributes its products through third-party distributors. It has collaborations with F.
Hoffman-La Roche Ltd., Hoffman-La Roche Inc., the SMA Foundation, National Taiwan University, Akcea Therapeutics, Inc., and Shiratori Pharmaceutical Co., Ltd. The company has license and collaboration agreement with Novartis Pharmaceuticals Corporation to develop PTC518 Huntington's disease program.
It markets Upstaza, a gene therapy with the brand name Kebilidi in the United States. PTC Therapeutics, Inc. was incorporated in 1998 and is headquartered in Warren, New Jersey.
| Country | United States |
| Founded | 1998 |
| IPO Date | Jun 20, 2013 |
| Industry | Biotechnology |
| Sector | Healthcare |
| Employees | 939 |
| CEO | Matthew Klein |
Contact Details
Address: 500 Warren Corporate Center Drive Warren, New Jersey 07059 United States | |
| Phone | 908 222 7000 |
| Website | ptcbio.com |
Stock Details
| Ticker Symbol | PTCT |
| Exchange | NASDAQ |
| Stock Type | Common Stock |
| Fiscal Year | January - December |
| Reporting Currency | USD |
| CIK Code | 0001070081 |
| CUSIP Number | 69366J200 |
| ISIN Number | US69366J2006 |
| Employer ID | 04-3416587 |
| SIC Code | 2834 |
Key Executives
| Name | Position |
|---|---|
| Matthew Klein | Chief Executive Officer |
| Pierre Gravier | Chief Financial Officer |
Latest SEC Filings
| Date | Type | Title |
|---|---|---|
| Oct 7, 2025 | 144 | Filing |
| Oct 6, 2025 | 144 | Filing |
| Oct 3, 2025 | 144 | Filing |
| Oct 3, 2025 | 144 | Filing |
| Oct 3, 2025 | 144 | Filing |
| Oct 3, 2025 | 144 | Filing |
| Sep 12, 2025 | 144 | Filing |
| Sep 11, 2025 | 144 | Filing |
| Sep 11, 2025 | 144 | Filing |
| Sep 9, 2025 | 144 | Filing |