Ultragenyx Pharmaceutical Inc. (RARE)

NASDAQ: RARE · Real-Time Price · USD
46.94
+0.54 (1.16%)
Nov 21, 2024, 10:49 AM EST - Market open
1.16%
Market Cap 4.32B
Revenue (ttm) 522.75M
Net Income (ttm) -558.99M
Shares Out 92.28M
EPS (ttm) -6.43
PE Ratio n/a
Forward PE n/a
Dividend n/a
Ex-Dividend Date n/a
Volume 86,285
Open 46.02
Previous Close 46.40
Day's Range 45.91 - 46.95
52-Week Range 37.02 - 60.37
Beta 0.58
Analysts Strong Buy
Price Target 86.79 (+85.53%)
Earnings Date Nov 5, 2024

About RARE

Ultragenyx Pharmaceutical Inc., a biopharmaceutical company, focuses on the identification, acquisition, development, and commercialization of novel products for the treatment of rare and ultra-rare genetic diseases in North America, Latin America, Japan, Europe, and internationally. Its biologic products include Crysvita (burosumab), an antibody targeting fibroblast growth factor 23 for the treatment of X-linked hypophosphatemia, as well as tumor-induced osteomalacia; Mepsevii, an enzyme replacement therapy for the treatment of children and ad... [Read more]

Industry Biotechnology
Sector Healthcare
IPO Date Jan 31, 2014
Employees 1,276
Stock Exchange NASDAQ
Ticker Symbol RARE
Full Company Profile

Financial Performance

In 2023, Ultragenyx Pharmaceutical's revenue was $434.25 million, an increase of 19.52% compared to the previous year's $363.33 million. Losses were -$606.64 million, -14.25% less than in 2022.

Financial Statements

Analyst Forecast

According to 14 analysts, the average rating for RARE stock is "Strong Buy." The 12-month stock price forecast is $86.79, which is an increase of 85.53% from the latest price.

Price Target
$86.79
(85.53% upside)
Analyst Consensus: Strong Buy
Stock Forecasts

News

Ultragenyx Reports Inducement Grant Under Nasdaq Listing Rule 5635(c)(4)

NOVATO, Calif., Nov. 20, 2024 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE), a biopharmaceutical company focused on the development and commercialization of novel therapies for rar...

18 hours ago - GlobeNewsWire

Ultragenyx: Ready For More Growth After Q3 Earnings Beat

Ultragenyx's strong Q3 earnings report, with a 42% YoY revenue increase, has reignited my interest in initiating a starter position in RARE. The company's promising pipeline, including late-stage prog...

8 days ago - Seeking Alpha

Ultragenyx Presents Positive Update on GTX-102 Angelman Syndrome Program at FAST's 17th Annual Global Science Summit

Phase 1/2 data show improvements across all domains and confirm that Phase 3 Aspire study is amply powered to establish efficacy of GTX-102

12 days ago - GlobeNewsWire

Ultragenyx Pharmaceutical Inc. (RARE) Q3 2024 Earnings Call Transcript

Ultragenyx Pharmaceutical Inc. (NASDAQ:RARE) Q3 2024 Earnings Conference Call November 5, 2024 5:00 PM ET Company Participants Joshua Higa - VP, IR Emil Kakkis - CEO and President Erik Harris - CCO H...

15 days ago - Seeking Alpha

Ultragenyx Reports Third Quarter 2024 Financial Results and Corporate Update

Third quarter 2024 total revenue grew 42% versus prior year to $139 million, including Crysvita® revenue of $98 million and Dojolvi® revenue of $21 million

15 days ago - GlobeNewsWire

Ultragenyx Provides Update on Stage 1 Cohorts in Pivotal Phase 1/2/3 Cyprus2+ Study Evaluating UX701 Gene Therapy for the Treatment of Wilson Disease

NOVATO, Calif., Oct. 03, 2024 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE) today reported that the Phase 1/2/3 Cyprus 2+ study of its UX701 gene therapy has demonstrated meaningfu...

6 weeks ago - GlobeNewsWire

Ultragenyx Announces Upcoming Setrusumab (UX143) Presentations at the ASBMR 2024 Annual Meeting

NOVATO, Calif., Sept. 26, 2024 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE) today announced that it will present seven abstracts related to its ongoing late-stage program evaluati...

2 months ago - GlobeNewsWire

Ultragenyx to Participate in Investor Conferences in September

Morgan Stanley 22 nd Annual Global Healthcare Conference on September 4 Cantor Global Healthcare Conference on September 17 Bank of America Global Healthcare Conference on September 18 NOVATO, Calif.,...

2 months ago - GlobeNewsWire

Ultragenyx's Strong Pipeline And Valuation Concerns: A Balanced Perspective

Ultragenyx develops therapies for rare genetic diseases, with a portfolio including Crysvita, Mepsevii, Dojolvi, and Evkeeza. The company's promising pipeline targets severe diseases like osteogenesis...

3 months ago - Seeking Alpha

Ultragenyx Pharmaceutical Inc. (RARE) Q2 2024 Earnings Call Transcript

Ultragenyx Pharmaceutical Inc. (NASDAQ:RARE) Q2 2024 Earnings Conference Call August 1, 2024 5:00 PM ET Company Participants Joshua Higa - Vice President, Investor Relations Emil Kakkis - Chief Execu...

3 months ago - Seeking Alpha

Amlogenyx Inc. Closes Successful Seed Funding Led by GordonMD® Global Investments LP

BEVERLY HILLS, Calif.--(BUSINESS WIRE)--GordonMD® Global Investments LP announced today that Amlogenyx Inc. has completed a seed funding round of USD 14 million. Amlogenyx, a subsidiary of Ultragenyx ...

3 months ago - Business Wire

Ultragenyx Reports Second Quarter 2024 Financial Results and Corporate Update

Second quarter total revenue of $147 million, Crysvita® revenue of $114 million and Dojolvi® revenue of $19 million

3 months ago - GlobeNewsWire

Ionis' Rare Development Disorder Drug Candidate 'Could Be Differentiated' From Peer Ultragenyx: Analyst

Ionis Pharmaceuticals Inc IONS released results Monday from the completed multiple ascending dose (MAD) portion of the Phase 1/2 open-label study of ION582 in people with Angelman syndrome (AS).

Other symbols: IONS
4 months ago - Benzinga

Ultragenyx Announces Pricing of Public Offering of Common Stock and Pre-Funded Warrants

NOVATO, Calif., June 13, 2024 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE), a biopharmaceutical company focused on the development and commercialization of novel therapies for ser...

5 months ago - GlobeNewsWire

Ultragenyx Announces Proposed Public Offering of Common Stock and Pre-Funded Warrants

NOVATO, Calif., June 12, 2024 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE), a biopharmaceutical company focused on the development and commercialization of novel therapies for ser...

5 months ago - GlobeNewsWire

Ultragenyx Announces Plans to File for Accelerated Approval of UX111 for the Treatment of Sanfilippo Syndrome Type A (MPS IIIA)

Agreement reached with FDA that cerebral spinal fluid (CSF) heparan sulfate (HS) can be used as a reasonable surrogate endpoint for accelerated approval

5 months ago - GlobeNewsWire

Ultragenyx and Mereo BioPharma Announce New Phase 2 Data from Phase 2/3 Orbit Study Demonstrating Sustained Reductions in Fracture Rates Following Treatment with Setrusumab (UX143) in Patients with Osteogenesis Imperfecta (OI)

14-month data show treatment with setrusumab resulted in  a large, sustained 67% reduction in annualized fracture rate  and persistent median annualized fracture rate of 0.00 (p=0.0014)

5 months ago - GlobeNewsWire

Ultragenyx: Modest Sales Growth, With Multiple Inflection Points Approaching

Ultragenyx Pharmaceutical Inc. revenues from regulatory approved drugs in Q1 of 2024 were $109 million, representing sales growth of 8% compared to the same time period in 2023. Setrusumab is an anti-...

5 months ago - Seeking Alpha

Ultragenyx to Participate at Goldman Sachs 45th Annual Global Healthcare Conference

NOVATO, Calif., June 04, 2024 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE), a biopharmaceutical company focused on the development and commercialization of novel therapies for ser...

6 months ago - GlobeNewsWire

Ultragenyx Announces Positive Top-Line Results from Phase 3 Study of DTX401 Gene Therapy for Glycogen Storage Disease Type Ia (GSDIa)

Treatment with DTX401 resulted in a statistically significant reduction in daily cornstarch intake at Week 48 (p

6 months ago - GlobeNewsWire

Ultragenyx to Participate at Bank of America's 2024 Healthcare Conference

NOVATO, Calif., May 07, 2024 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE), a biopharmaceutical company focused on the development and commercialization of novel therapies for seri...

7 months ago - GlobeNewsWire

Ultragenyx Pharmaceutical, Inc. (RARE) Q1 2024 Earnings Call Transcript

Ultragenyx Pharmaceutical, Inc. (NASDAQ:RARE) Q1 2024 Earnings Conference Call May 2, 2024 5:00 PM ET Company Participants Joshua Higa - Vice President of Investor Relations Emil Kakkis - Chief Execu...

7 months ago - Seeking Alpha

Ultragenyx Reports First Quarter 2024 Financial Results and Corporate Update

First quarter total revenue of $109 million, Crysvita® revenue of $83 million and Dojolvi® revenue of $16 million

7 months ago - GlobeNewsWire

Ultragenyx Issues 2023 Corporate Responsibility Report, Showcasing Commitment to Improving Equity and Access to Innovation in Rare Disease

NOVATO, Calif., April 30, 2024 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE) today released its 2023 Corporate Responsibility Report, which showcases the company's efforts to trans...

7 months ago - GlobeNewsWire

Ultragenyx to Host Conference Call for First Quarter 2024 Financial Results and Corporate Update

NOVATO, Calif., April 25, 2024 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE), a biopharmaceutical company focused on the development and commercialization of novel products for ser...

7 months ago - GlobeNewsWire