| 1 | TVTX | Travere Therapeutics, Inc. | 3.28% |
| 2 | IONS | Ionis Pharmaceuticals, Inc. | 3.21% |
| 3 | INSM | Insmed Incorporated | 2.97% |
| 4 | MDGL | Madrigal Pharmaceuticals, Inc. | 2.78% |
| 5 | AUPH | Aurinia Pharmaceuticals Inc. | 2.71% |
| 6 | TARS | Tarsus Pharmaceuticals, Inc. | 2.70% |
| 7 | TBPH | Theravance Biopharma, Inc. | 2.65% |
| 8 | BBIO | BridgeBio Pharma, Inc. | 2.51% |
| 9 | ROIV | Roivant Sciences Ltd. | 2.51% |
| 10 | LGND | Ligand Pharmaceuticals Incorporated | 2.46% |
| 11 | RYTM | Rhythm Pharmaceuticals, Inc. | 2.40% |
| 12 | UTHR | United Therapeutics Corporation | 2.35% |
| 13 | PTCT | PTC Therapeutics, Inc. | 2.33% |
| 14 | FOLD | Amicus Therapeutics, Inc. | 2.23% |
| 15 | ARDX | Ardelyx, Inc. | 2.16% |
| 16 | PHAT | Phathom Pharmaceuticals, Inc. | 2.15% |
| 17 | KRYS | Krystal Biotech, Inc. | 2.15% |
| 18 | KNSA | Kiniksa Pharmaceuticals International, plc | 2.12% |
| 19 | INCY | Incyte Corporation | 2.09% |
| 20 | REGN | Regeneron Pharmaceuticals, Inc. | 2.07% |
| 21 | MIRM | Mirum Pharmaceuticals, Inc. | 2.06% |
| 22 | ALNY | Alnylam Pharmaceuticals, Inc. | 2.05% |
| 23 | AXSM | Axsome Therapeutics, Inc. | 1.97% |
| 24 | DAWN | Day One Biopharmaceuticals, Inc. | 1.96% |
| 25 | BIIB | Biogen Inc. | 1.90% |
| View BBP holdings |